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Repligen has reported positive results from Phase I study of RG3039 for the potential treatment of spinal muscular atrophy (SMA). The blinded, ascending, single dose study demonstrated that RG3039 was well tolerated at all doses administered and showedIf you were asked which genetic disease is the number one cause of death among babies in the United States, chances are spinal muscular atrophy wouldLatest News The Fifth Annual Walk n' Roll to cure Spinal Muscular Atrophy (SMA) in honor of

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