Spinal Muscular Atrophy: Avery's Bucket List: Parents pen blog for baby dying of spinal muscular atrophy

Spinal Muscular Atrophy Spinal Muscular Atrophy: 335.10 - Spinal Muscular Atrophy, Unspecified: 335.19 - Spinal Muscular Atrophy, Other Adult Spinal Muscular.Repligen licensed RG3039 in 2009 from Families of Spinal Muscular Atrophy (FSMA), a patient advocacy organization that funded and directed the preclinical development of RG3039 with an investment of more than $13 million.Diagnosed with spinal muscular atrophy type 1, Avery Canahuati was told she has only 13 months left to live. Tweets

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