Spinal Muscular Atrophy: Avery's Bucket List: Parents pen blog for baby dying of spinal muscular atrophy

The research may lead to treatment for infected individuals and also increase the understanding of genetic diseases such as amyotrophic lateral sclerosis (ALS; Lou Gehrig's disease) and spinal muscular atrophy (SMA), the leading genetic cause of infantIn addition, "I plan to discuss strategic alternatives for Repligen in light of the positive Phase 1 results of 3039 for the potential treatment of Spinal Muscular Atrophy (SMA), and the decision of the FDA to require additional clinical

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